Gene Therapy for HD: Sorting Truth from Hype – 7/22 1PM ET

Edith Pfister, Ph.D., Assistant Professor, University of Massachusetts Medical

This talk will cover the basics of therapies designed to lower huntingtin: what do we know and what don’t we know. It will introduce the basic mechanisms of huntingtin lowering and gene therapy. The goal is to introduce the language of huntingtin lowering and of gene therapy and to come away with a basic understanding of how they work.